Member Roster
Below is a comprehensive list of Community Congress members. Each working group is co-chaired by a patient organization participant and industry participant. Working groups engage on an ongoing basis and meet annually in December in Washington, DC. Ultimately, Community Congress serves as a platform for engagement with rare disease stakeholders and provides critical guidance to the Foundation and leadership to the rare disease community.
For additional information on the Foundation’s Community Congress program or to join the Community Congress, please visit the program’s homepage.
A roster of all Member Organizations in the Community Congress. Please click through the other tabs to see the composition of each Working Group.
| Type | Organization |
|---|---|
| Industry | Acadia Pharmaceuticals |
| Patient Organization | Acid Maltase Deficiency Association (AMDA) |
| Patient Organization | Acromegaly Community, Inc |
| Patient Organization | ADNP Kids Research Foundation |
| Patient Organization | Adrenal Insufficiency United |
| Industry | AdvaMed |
| Patient Organization | Advocacy & Awareness for Immune Disorders Association |
| Industry | AdvocacyWorks |
| Industry | Agios Pharmaceuticals |
| Patient Organization | Aislinn’s Wish Foundation |
| Industry | Akouos |
| Patient Organization | Alagille Syndrome Foundation |
| Patient Organization | ALD Alliance |
| Patient Organization | ALD Connect |
| Industry | Alexion Pharmaceuticals |
| Industry | Alkermes |
| Patient Organization | All Things Kabuki |
| Other Partner | Alliance for Patient Access |
| Other Partner | Alliance for Regenerative Medicine |
| Industry | Alnylam Pharmaceuticals |
| Patient Organization | Alpha-1 Foundation |
| Patient Organization | Alport Syndrome Foundation |
| Patient Organization | American Adrenal Association |
| Patient Organization | American Behcet’s Disease Association |
| Patient Organization | American Bone Health |
| Patient Organization | American Kidney Fund |
| Patient Organization | American Liver Foundation |
| Patient Organization | American Porphyria Foundation |
| Industry | Amgen |
| Industry | Amicus Therapeutics |
| Patient Organization | Amour Science Foundation |
| Patient Organization | Amyloidosis Foundation |
| Patient Organization | Amyloidosis Research Consortium |
| Patient Organization | AnCan |
| Patient Organization | Angelman Syndrome Foundation |
| Patient Organization | APBD Research Foundation |
| Patient Organization | Appendix Cancer/Psuedomyxoma Peritonei Research Foundation (ACPMP) |
| Industry | Applied Therapeutics |
| Industry | Arcturus Therapeutics |
| Industry | Argenx |
| Industry | Ascendis Pharma, Inc. |
| Patient Organization | Ashley House |
| Patient Organization | Association for Creatine Deficiencies |
| Industry | Astellas |
| Industry | Astria Therapeutics |
| Patient Organization | Autism Science Foundation |
| Patient Organization | Autoimmune Association |
| Patient Organization | Autoimmune Community Institute |
| Patient Organization | Autoinflammatory Alliance |
| Patient Organization | Avery’s Hope |
| Industry | Avidity Biosciences |
| Patient Organization | AXYS |
| Industry | Azafaros |
| Patient Organization | BARE Inc |
| Patient Organization | Barth Syndrome Foundation |
| Patient Organization | BDSRA Foundation |
| Industry | Beren Therapeutics |
| Patient Organization | Best Day Ever Foundation |
| Industry | BIO |
| Industry | BioCryst |
| Industry | Biogen |
| Industry | BioLaunch Solutions |
| Industry | BioMarin Pharmaceutical Inc |
| Industry | Blueprint Medicines |
| Industry | Boehringer Ingelheim |
| Patient Organization | Boomer Esiason Foundation |
| Patient Organization | Born a Hero Research Foundation |
| Patient Organization | BPAN Warriors |
| Industry | BridgeBio |
| Patient Organization | C-Path |
| Patient Organization | Cal Rare |
| Industry | California Life Sciences |
| Other | Canary Advisors |
| Patient Organization | CARES Foundation, Inc. |
| Patient Organization | Castleman Disease Collaborative Network |
| Patient Organization | CDG CARE |
| Patient Organization | Center for Innovation and Value Research (formerly IVI) |
| Patient Organization | CFC International |
| Industry | Chiesi USA, Inc. |
| Patient Organization | Child Neurology Foundation |
| Patient Organization | Children’s PKU Network |
| Patient Organization | Chondrosarcoma CS Foundation |
| Patient Organization | Choroideremia Research Foundation |
| Other Partner | Clinical and Laboratory Standards Institute (CLSI) |
| Patient Organization | Color of Crohn’s and Chronic Illness |
| Patient Organization | Congenital Hyperinsulinism International |
| Patient Organization | Conquer MG |
| Patient Organization | COPD Foundation – Bronchiectasis & NTM Intiative |
| Patient Organization | Costello Syndrome Family Network |
| Industry | Creyone Bio, Inc |
| Industry | Crinetics Pharmaceutical |
| Industry | CSL Behring |
| Patient Organization | Cure CMD |
| Patient Organization | CURE GABA-A |
| Patient Organization | Cure GM1 Foundation |
| Patient Organization | Cure LGMD2i Foundation |
| Patient Organization | Cure Mito Foundation |
| Patient Organization | Cure Sanfilippo Foundation |
| Patient Organization | Cure SMA |
| Patient Organization | Cure VCP Disease, Inc. |
| Patient Organization | CureDuchenne |
| Patient Organization | Curing Retinal Blindness Foundation |
| Patient Organization | Cyclic Vomiting Syndrome Association |
| Patient Organization | Cystic Fibrosis Research Institute |
| Patient Organization | Cystinosis Research Network |
| Patient Organization | Dana’s Angels Research Trust |
| Patient Organization | Danny’s Dose Alliance, Inc |
| Patient Organization | debra of America |
| Industry | Denali Therapeutics |
| Patient Organization | Dravet Syndrome Foundation |
| Patient Organization | Dreamsickle Kids Foundation |
| Patient Organization | E.WE Foundation |
| Patient Organization | EB Research Partnership |
| Patient Organization | ECD Global Alliance |
| Industry | Edgewise Therapeutics |
| Patient Organization | ELI Foundation Puerto Rico |
| Industry | Eli Lilly and Company |
| Industry | Elpida Therapeutics |
| Patient Organization | Endosalpingiosis Foundation |
| Industry | Entrada Therapeutics |
| Patient Organization | Eosinophilic & Rare Disease Cooperative |
| Other Partner | Every Cure |
| Industry | Exact Sciences |
| Patient Organization | Expecting Health |
| Patient Organization | Fabry Support & Information Group |
| Patient Organization | Family Heart Foundation |
| Patient Organization | FD/MAS Alliance |
| Patient Organization | Fibromuscular Dysplasia Society of America |
| Patient Organization | Fighting for Kaiden Foundation |
| Patient Organization | FOP Association |
| Industry | Forge Biologics |
| Patient Organization | Foundation Fighting Blindness |
| Patient Organization | Foundation for Angelman Syndrome Therapeutics (FAST) |
| Patient Organization | Foundation for Sarcoidosis Research (FSR) |
| Patient Organization | Foundation to fight H-ABC |
| Patient Organization | Friedreich’s Ataxia Research Alliance (FARA) |
| Industry | Fulcrum Therapeutics |
| Patient Organization | g6pd Deficiency Foundation |
| Patient Organization | Galactosemia Foundation |
| Patient Organization | GBS|CIDP Foundation Int’l |
| Patient Organization | Gene Giraffe Project |
| Industry | GeneDx |
| Industry | Genentech |
| Industry | GlaxoSmithKline |
| Patient Organization | Global Foundation for Peroxisomal Diseases |
| Patient Organization | Global Genes |
| Patient Organization | Global Liver Institute |
| Patient Organization | GRIN2B Foundation |
| Patient Organization | Hairy Cell Leukemia Foundation |
| Patient Organization | HCU Network America |
| Patient Organization | Hemophilia Council of California |
| Patient Organization | Hemophilia Federation of America |
| Patient Organization | Hermansky-Pudlak Syndrome (HPS) Network |
| Patient Organization | Histiocytosis Association |
| Patient Organization | Hope for Dante’ – Batten Disease Awareness |
| Patient Organization | Hunter’s Hope Foundation |
| Patient Organization | Huntington’s Disease Society of America (HDSA) |
| Industry | Hyman, Phelps & McNamara, P.C. |
| Patient Organization | Hypersomnia Foundation |
| Patient Organization | I Am ALS |
| Patient Organization | Immune Deficiency Foundation |
| Industry | Immunovant |
| Other | Innov8 Health Policy, LLC |
| Industry | Insmed |
| Industry | Institute for Gene Therapies |
| Patient Organization | International Cystinuria Foundation |
| Patient Organization | International Foundation for CDKL5 Research |
| Patient Organization | International Pemphigus and Pemphigoid Foundation |
| Patient Organization | International Rett Syndrome Foundation |
| Patient Organization | International Waldenstrom’s Macroglobulinemia Foundation (IWMF) |
| Industry | Invitae |
| Industry | Ionis Pharmaceuticals |
| Industry | Ipsen |
| Industry | IQVIA |
| Patient Organization | Jack McGovern Coats Disease Foundation |
| Patient Organization | Jansen’s Foundation |
| Industry | Jazz Therapeutics |
| Patient Organization | Jett Foundation |
| Industry | Johnson and Johnson Healthcare Systems |
| Patient Organization | Jonah’s Just Begun – Curing SanFilippo Disease One Day at a Time |
| Patient Organization | Jordan’s Guardian Angels |
| Patient Organization | Joshua Frase Foundation |
| Patient Organization | Juju and Friends CLN2 Warrior Foundation |
| Industry | Kith Collective |
| Patient Organization | KrabbeConnect |
| Patient Organization | Krishnan Family Foundation |
| Industry | Kyowa Kirin |
| Patient Organization | LGMD2D Foundation |
| Patient Organization | Li-Fraumeni Syndrome Association |
| Patient Organization | Lipodystrophy United |
| Patient Organization | Little Hercules Foundation |
| Patient Organization | Little Miss Hannah Foundation |
| Patient Organization | Littlest Tumor Foundation |
| Industry | Longboard Pharmaceuticals |
| Patient Organization | Lowe Syndrome Association |
| Patient Organization | Lung Transplant Foundation |
| Patient Organization | Lupus Foundation of America |
| Patient Organization | Lymphangiomatosis & Gorham’s Disease Alliance (LGDA) |
| Patient Organization | Mac Pact |
| Industry | Mahzi Therapeutics |
| Industry | Mallinckrodt Pharmaceuticals |
| Patient Organization | March of Dimes |
| Industry | Marinus Pharmaceuticals |
| Patient Organization | Martin Center Sickle Cell Initiative |
| Patient Organization | MarylandRARE |
| Industry | Merck |
| Patient Organization | Minutes Matter – MCADD |
| Patient Organization | Mission MSA |
| Patient Organization | Mission: Cure |
| Patient Organization | Mississippi Metabolics Foundation |
| Patient Organization | MitoAction |
| Patient Organization | MLD Foundation |
| Patient Organization | MTM-CNM Family Connection |
| Patient Organization | MTS Sickle Cell Foundation, Inc. |
| Patient Organization | Muscular Dystrophy Association (MDA) |
| Patient Organization | Myasthenia Gravis Association |
| Patient Organization | Myasthenia Gravis Foundation of America |
| Patient Organization | Myositis Support and Understanding Association |
| Patient Organization | Narcolepsy Network |
| Patient Organization | National Alliance for Caregiving (NAC) |
| Patient Organization | National Ataxia Foundation |
| Patient Organization | National Bleeding Disorders Foundation (formerly NHF) |
| Patient Organization | National Foundation for Ectodermal Dysplasias |
| Patient Organization | National Fragile X Foundation |
| Patient Organization | National Health Council |
| Patient Organization | National Leiomyosarcoma Foundation |
| Patient Organization | National Lymphedema Network |
| Patient Organization | National MPS (Mucopolysaccharidoses) Society |
| Patient Organization | National Niemann-Pick Disease Foundation (NNPDF) |
| Industry | National Pharmaceutical Council |
| Patient Organization | National PKU Alliance |
| Patient Organization | National Scleroderma Foundation |
| Industry | National Society of Genetic Counselors (NSGC) |
| Patient Organization | National Tay-Sachs & Allied Diseases Association (NTSAD) |
| Patient Organization | National Tay-Sachs & Allied Diseases Association (NTSAD) |
| Patient Organization | NephCure for Rare Kidney Disease |
| Patient Organization | Network of Tyrosinemia Advocates |
| Industry | Neurocrine Biosciences |
| Patient Organization | Neuroimmune Foundation |
| Patient Organization | Neuromuscular Disease Foundation |
| Industry | Novartis |
| Industry | Novo Nordisk |
| Industry | NS Pharma |
| Patient Organization | NTM Info & Research, Inc. |
| Patient Organization | NW Rare Disease Coalition |
| Industry | Orchard Therapeutics |
| Patient Organization | Organic Acidemia Association |
| Industry | Otsuka |
| Industry | Ovid Therapeutics |
| Patient Organization | Oxalosis and Hyperoxaluria Foundation |
| Patient Organization | Pachyonychia Congenita Project |
| Patient Organization | Parent Project Muscular Dystrophy (PPMD) |
| Industry | Parexel |
| Patient Organization | Partnership to Fight Chronic Disease (PFCD) |
| Other Partner | Partnership to Improve Patient Care |
| Patient Organization | Pediatric Hydrocephalus Foundation |
| Patient Organization | People With Empathy |
| Industry | PepGen |
| Industry | Personalized Medicine Coalition |
| Patient Organization | Petronille Healthy Society |
| Patient Organization | PFIC Network, Inc. |
| Industry | Pfizer, Inc. |
| Industry | Pharming Healthcare Inc. |
| Industry | PhRMA |
| Patient Organization | Piper’s Kidney Beans |
| Patient Organization | PMG Awareness Organization |
| Patient Organization | Pompe Alliance |
| Patient Organization | Prader-Willi Syndrome Association (PWSA) |
| Patient Organization | Project Alive |
| Patient Organization | PSC Partners Seeking a Cure |
| Industry | PTC Therapeutics |
| Patient Organization | PTEN Hamartoma Tumor Syndrome Foundation |
| Patient Organization | Pulmonary Fibrosis Foundation |
| Patient Organization | Pulmonary Hypertension Association |
| Industry | PWR |
| Other Partner | Rare Access Action Project |
| Patient Organization | Rare And Black |
| Patient Organization | Rare and Undiagnosed Network |
| Industry | Rare Disease Company Coalition (RDCC) |
| Patient Organization | Rare Disease Innovations Institute, Inc. |
| Patient Organization | Rare KC |
| Patient Organization | Rare New England |
| Patient Organization | RareConnect.org |
| Patient Organization | RASOPATHIES Network |
| Industry | REGENXBIO, Inc. |
| Patient Organization | Remember the Girls |
| Other | Reservior Communications Group |
| Industry | Revvity, Inc. |
| Industry | Rhythm Pharmaceuticals |
| Patient Organization | RSDSA.org |
| Patient Organization | Ryan Foundation |
| Patient Organization | RYR-1 Foundation |
| Industry | Sanofi |
| Patient Organization | Sarcoma Foundation of America |
| Industry | Sarepta Therapeutics |
| Patient Organization | SCAD Alliance |
| Industry | Scholar Rock |
| Patient Organization | SCID, Angels for Life Foundation |
| Industry | Servier |
| Patient Organization | Sick Cells |
| Patient Organization | Sickle Cell Association of Kentuckiana |
| Patient Organization | Sickle Cell Consortium |
| Patient Organization | Sickle Cell Disease Association of America |
| Patient Organization | Sickle Cell Foundation of Tennessee |
| Patient Organization | Sickle Cell Support Services |
| Patient Organization | Sister’s Hope Foundation for Hereditary Diffuse Leukoencephalopathy |
| Patient Organization | SLC6A1 Connect |
| Patient Organization | Smashing Walnuts |
| Industry | Soleno Therapeutics |
| Industry | Spark Therapeutics |
| Patient Organization | Spastic Paraplegia Foundation, Inc. |
| Patient Organization | Spina Bifida Association |
| Patient Organization | SSADH Association |
| Industry | Stoke Therapeutics |
| Patient Organization | Stronger Than Sarcoidosis |
| Patient Organization | STXBP1 Foundation |
| Patient Organization | Sudden Arrhythmia Death Syndromes (SADS) Foundation |
| Industry | Sumitomo Pharma America |
| Patient Organization | Super T’s Mast Cell Foundation |
| Patient Organization | Supporters of Families with Sickle Cell Disease, Inc. |
| Patient Organization | SynGAP Research Fund, Inc. |
| Patient Organization | SYNGAP1 Foundation |
| Patient Organization | T.E.A.M. 4 Travis (Together Ending Asplenia Mortality) |
| Industry | Takeda Pharmaceuticals |
| Patient Organization | TANC2 Foundation |
| Patient Organization | Taylor’s Tale |
| Patient Organization | Team Joseph |
| Patient Organization | Team Telomere |
| Patient Organization | Team Titin, Inc. |
| Patient Organization | Texas Rare Alliance |
| Patient Organization | The Akari Foundation |
| Patient Organization | The ALS Association |
| Other Partner | The Assistance Fund |
| Patient Organization | The Association for Frontotemporal Degenerations |
| Patient Organization | The Bluefield Project to Cure Frontotemporal Dementia |
| Patient Organization | The Bonnell Foundation: Living with Cystic Fibrosis |
| Patient Organization | The Bow Foundation |
| Patient Organization | The Calliope Joy Foundation |
| Patient Organization | The Ehlers-Danos Society |
| Patient Organization | The Firefly Fund |
| Patient Organization | The Julius Louis Happy Little Guy Foundation, Inc. |
| Patient Organization | The LAM Foundation |
| Patient Organization | The Lambert-Eaton LEMS Family Association |
| Patient Organization | The Mast Cell Disease Society |
| Patient Organization | The Myositis Association |
| Patient Organization | The Newborn Foundation |
| Patient Organization | The Speak Foundation |
| Industry | Travere Therapeutics |
| Industry | Ultragenyx |
| Patient Organization | Undiagnosed Diseases Network (UDN) |
| Patient Organization | Undiagnosed Diseases Network Foundation (UDNF) |
| Patient Organization | United Leukodystrophy Foundation |
| Patient Organization | United Mitochondrial Disease Foundation |
| Patient Organization | United MSD Foundation |
| Other | United Parcel Service (UPS) |
| Patient Organization | Uriel Owens Sickle Cell Disease Association of the Midwest |
| Patient Organization | US Hereditary Angioedema Association |
| Patient Organization | US Thrombotic Microangiopathy Alliance (USTMA) |
| Patient Organization | Vasculitis Foundation |
| Industry | Vertex Pharmaceuticals |
| Industry | Vigil Neuroscience |
| Industry | Viridian Therapeutics |
| Industry | Wave Life Sciences |
| Industry | WCG Clinical |
| Patient Organization | Williams Syndrome Association |
| Patient Organization | Wylder Nation Foundation |
| Industry | Zambon |
| Industry | Zevra |
| Patient Organization | ZTTK SON-Shine Foundation |