This resource explores how PDUFA has helped strengthen FDA review processes, accelerate innovation, and support the development of therapies for rare diseases. It also discusses the importance of continued investment in regulatory infrastructure and patient-focused drug development.
New Name, Same Commitment to Rare Diseases
The EveryLife Foundation for Rare Diseases has become The RARE Foundation! Read more about our new brand and how it unifies our advocacy work on behalf of the rare disease community.
